Citeline&ASGCT：2025年第一季度基因、细胞和RNA疗法概况报告（英文版）

One new approved advanced therapy for each of the gene, cell, and RNA categories occurred in Q1 2025 • In the US: Neurotech’s Encelto, an intraocular implant of encapsulated engineered human cells, was approved for the treatment of macular telangiectasia type 2 (MacTel); Alnylam’s siRNA therapy, Qfitlia was approved for the treatment of hemophilia A or B • China’s NMPA approves the country’s first mesenchymal stem cell therapy, Platinum Life’s Ruibosheng, indicated for steroid-refractory acut